Projects per year
Fingerprint
- 1 Similar Profiles
Collaborations and top research areas from the last five years
Projects
- 1 Active
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IOF3008: IOF GEAR: Regenerate: development and validation of next-generation gene therapy
VandenDriessche, T., Chuah, M. & Pham, H. Q.
1/01/19 → 31/12/25
Project: Applied
Research output
- 6 Article
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Treatment of Infantile-Onset Pompe Disease in a Rat Model with Muscle-Directed AAV Gene Therapy
Muñoz, S., Bertolin, J., Jimenez, V., Jaén, M. L., Garcia, M., Pujol, A., Vilà, L., Sacristan, V., Barbon, E., Ronzitti, G., El Andari, J., Tulalamba, W., Pham, Q. H., Ruberte, J., VandenDriessche, T., Chuah, M. K., Grimm, D., Mingozzi, F. & Bosch, F., Mar 2024, In: Molecular Metabolism. 81, 13 p., 101899.Research output: Contribution to journal › Article › peer-review
Open Access6 Citations (Scopus) -
Semirational bioengineering of AAV vectors with increased potency and specificity for systemic gene therapy of muscle disorders
El Andari, J., Renaud-Gabardos, E., Tulalamba, W., Weinmann, J., Mangin, L., Pham, Q. H., Hille, S., Bennett, A., Attebi, E., Bourges, E., Leborgne, C., Guerchet, N., Fakhiri, J., Krämer, C., Wiedtke, E., McKenna, R., Guianvarc'h, L., Toueille, M., Ronzitti, G., Hebben, M., & 8 others , 23 Sept 2022, In: Science Advances. 8, 38, eabn4704.Research output: Contribution to journal › Article › peer-review
Open AccessFile41 Citations (Scopus)67 Downloads (Pure) -
Gene Therapy For Hemophilia B Using CB 2679d-GT: A Novel Factor IX Variant With Higher Potency Than Factor IX Padua
Nair, N., De Wolf, D., Nguyen, P. A., Pham, H. Q., Samara-Kuko, E., Landau, J., E.Blouse, G., Chuah, M. & VandenDriessche, T., 27 May 2021, In: Blood. 137, 21, p. 2902-2906 5 p.Research output: Contribution to journal › Article › peer-review
Open Access9 Citations (Scopus) -
Distinct transduction of muscle tissue in mice after systemic delivery of AAVpo1 vectors
Tulalamba, W., Weinmann, J., Pham, Q. H., El Andari, J., VandenDriessche, T., Chuah, M. K. & Grimm, D., Apr 2020, In: Gene Therapy. 27, 3-4, p. 170-179 10 p.Research output: Contribution to journal › Article › peer-review
9 Citations (Scopus) -
Identification of a myotropic AAV by massively parallel in vivo evaluation of barcoded capsid variants
Weinmann, J., Weis, S., Sippel, J., Tulalamba, W., Remes, A., El Andari, J., Herrmann, A-K., Pham, Q. H., Borowski, C., Hille, S., Schönberger, T., Frey, N., Lenter, M., VandenDriessche, T., Müller, O. J., Chuah, M. K., Lamla, T. & Grimm, D., 28 Oct 2020, In: Nature Communications. 11, 1, 5432.Research output: Contribution to journal › Article › peer-review
Open Access162 Citations (Scopus)
Datasets
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Treatment of infantile-onset Pompe disease in a rat model with muscle-directed AAV gene therapy
Pham, H. Q. (Creator), Molecular Metabolism, 2024
DOI: 10.1016/j.molmet.2024.101899
Dataset
File
Activities
- 3 Participation in conference
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EU H2020 project MYOCure: 3rd Progress Meeting
Hong Quang Pham (Participant)
28 Mar 2019 → 29 Mar 2019Activity: Participating in or organising an event › Participation in conference
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EU H2020 project Cardioregenix: Kick off meeting
Hong Quang Pham (Chair)
25 Feb 2019 → 26 Feb 2019Activity: Participating in or organising an event › Participation in conference
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MYOCURE 2nd progress meeting
Hong Quang Pham (Participant)
19 Mar 2018 → 20 Mar 2018Activity: Participating in or organising an event › Participation in conference