CRISPR/Cas9-mediated editing for dominant genetic disorders: efficient excision of trinucleotide repeat expansion in myotonic dystrophy

S. Dastidar, S. Ardui, K. Singh, N. Nair, Y. Fu, D. Reyon, E. Samara, M. F. M. Gerli, A. F. Klein, W. DeSchrijver, D. Majumdar, J. Tipanee, S. Seneca, W. Tulalamba, H. Wang, Y. C. Chai, P. In't Veld, D. Furling, F. S. Tedesco, J. R. VermeeschJ. K. Joung, M. K. Chuah, T. VandenDriessche

Research output: Contribution to journalMeeting abstract (Journal)

Original languageEnglish
Pages (from-to)A7-A7
JournalHuman Gene Therapy
Issue number12
Publication statusPublished - Dec 2017
EventESGCT XXV Anniversary Congress in Collaboration with the German Society for Gene Therapy October 17–20, 2017 Berlin, Germany: ESGCT XXV Congress - BERLIN, Germany
Duration: 17 Oct 201720 Oct 2017

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