CRISPR/Cas9-Mediated Editing of Trinucleotide Repeat Expansion in Myotonic Dystrophy

Sumitava Dastidar, Kshitiz Singh, Nisha Nair, Yanfang Fu, Deepak Reyon, Ermira Samara, Mattia F. M. Gerli, Arnaud F. Klein, Thomas Jans, Jaitip Tipanee, Sara Seneca, Warut Tulalamba, Hui Wang, Joris R. Vermeesch, Yoke Chin Chai, Peter In't Veld, Denis Furling, Francesco Saverio Tadesco, J. Keith Joung, Marinee K. L. ChuahThierry C. VandenDriessche

Research output: Contribution to journalMeeting abstract (Journal)

Original languageEnglish
Pages (from-to)85-85
Number of pages1
JournalMolecular Therapy
Issue number5
Publication statusPublished - May 2017
Event20th Annual Meeting of the American-Society-of-Gene-and-Cell-Therapy (ASGCT) - Washington, DC, United States
Duration: 10 May 201713 May 2017


  • Myotonic Dystrophy

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