Long-Term Functional Correction of Pompe Disease and Increased α-Glucosidase Expression after Gene Therapy with Novel Combinations of Muscle-Targeted Transcriptional Cis-Regulatory Elements
- QH Pham
- , VA Bheemsetty
- , PA Nguyen
- , E Samara-Kuko
- , FY Gao
- , MK Chuah
- , Thierry VandenDriessche
Onderzoeksoutput: Article › peer review
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